mRNA-3704

N/A

Report date: 2024/09/14 10:51:28

Base Information

Drug NamemRNA-3704
Drug Alias NameMUT mRNA therapy (lipid nanoparticles, methylmalonic Other Drug Names acidemia)mRNA-3704
ClassificationCell and gene therapy > Gene therapy > mRNA
Mechanisms of ActionMUT gene stimulants
TargetsMethylmalonyl-CoA Mutase
Therapy Area/IndicationsMethylmalonic acidaemiaMetabolism, Inborn Errors
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryN/A
CombinationsNo
Global Highest StatusDiscontinued (Phase 2 Clinical)
Highest Status in ChinaN/A
Originator CompaniesModerna Inc
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesModerna Inc
Active IndicationsN/A
Inactive IndicationsMethylmalonic acidaemiaMetabolism, Inborn Errors

Other Information

ATC CodeN/A
Related LinksN/A