Drisapersen

N/A

Report date: 2022/06/28 10:09:48
NME

Base Information

Drug NameDrisapersen
Drug Alias Name2'-O-methyl-phosphorothioate oligonucleotideKyndrisaH51-AON-23GSK-2402968GSK2402968A +[6
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionDystroglycan stimulants
TargetsDystroglycan
Therapy Area/IndicationsMuscular Dystrophy, DuchenneMuscular Dystrophies
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryCzechiaBelgiumBulgaria +[25
CombinationsNo
Global Highest StatusDiscontinued (NDA/BLA)
Highest Status in ChinaN/A
Originator CompaniesBiomarin Pharmaceutical Inc
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Active IndicationsN/A
Inactive IndicationsMuscular Dystrophy, DuchenneMuscular Dystrophies

Other Information

ATC CodeM09AX04
Related LinksWikipediaKEGG