hLB-001

N/A

Report date: 2023/10/26 17:04:40

Base Information

Drug NamehLB-001
Drug Alias NameLB-001hLB-001
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionGene transferenceMethylmalonyl-CoA Mutase stimulants
TargetsMethylmalonyl-CoA Mutase
Therapy Area/IndicationsMethylmalonic acidaemia
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusDiscontinued (Phase 2 Clinical)
Highest Status in ChinaN/A
Originator CompaniesLogicbio Therapeutics Inc
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Active IndicationsN/A
Inactive IndicationsMethylmalonic acidaemia

Other Information

ATC CodeN/A
Related LinksN/A