AXO-AAV-ALS

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Report date: 2025/12/12 17:31:46

Base Information

Drug NameAXO-AAV-ALS
Drug Alias NameAdeno associated virus vectored gene therapiesAXO-AAV-FTDAXO-AAV-TBD
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionGuanine nucleotide exchange C9orf72 modulators
TargetsGuanine nucleotide exchange C9orf72
Therapy Area/IndicationsAmyotrophic Lateral SclerosisDementia
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryN/A
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesBenitec Biopharma Ltd
China Registration ClassN/A

Develop Information

Active CompaniesBenitec Biopharma Ltd
Inactive CompaniesN/A
Active IndicationsAmyotrophic Lateral SclerosisDementia
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A