UX-053

N/A

Report date: 2026/04/07 20:00:20
NME

Base Information

Drug NameUX-053
Drug Alias NameLUNAR-GSD3LUNAR-GSDIIILUNAR-RAREUX-053
ClassificationCell and gene therapy > Gene therapy > mRNA
Mechanisms of ActionGene expression stimulantsGene transference
TargetsNot applicable
Therapy Area/IndicationsGlycogen Storage Disease Type III
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited StatesItalySpain
CombinationsNo
Global Highest StatusDiscontinued (Phase 2 Clinical)
Highest Status in ChinaN/A
Originator CompaniesArcturus Therapeutics Inc
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesUltragenyx Pharmaceutical Inc
Active IndicationsN/A
Inactive IndicationsGlycogen Storage Disease Type III

Other Information

ATC CodeN/A
Related LinksN/A