Clemidsogene lanparvovec

N/A

Report date: 2025/06/19 16:47:02

Base Information

Drug NameClemidsogene lanparvovec
Drug Alias NameRGX-121AAV9-IDSAAV9.hIDS
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector > AAV9 vector
Mechanisms of ActionIduronate-2-sulfatase gene transference
TargetsIduronate-2-sulfatase
Therapy Area/IndicationsMucopolysaccharidosis II
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryCanadaUnited StatesBrazil
CombinationsNo
Global Highest StatusNDA/BLA
Highest Status in ChinaN/A
Originator CompaniesRegenxbio Inc
China Registration ClassN/A

Develop Information

Active CompaniesRegenxbio IncNippon Shinyaku Co Ltd
Inactive CompaniesN/A
Active IndicationsMucopolysaccharidosis II
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A