PBGM-01

N/A

Report date: 2025/07/18 20:00:26

Base Information

Drug NamePBGM-01
Drug Alias Name腺相关病毒载体（AAV）基因递送疗法（Passage）PBGM-01
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector > AAVhu68 vector
Mechanisms of ActionGene transference
TargetsNot applicable
Therapy Area/IndicationsGangliosidosis, GM1Hereditary Central Nervous System Demyelinating Diseases
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited StatesTurkeyUnited Kingdom +[4] 
CombinationsNo
Global Highest StatusPhase 2 Clinical
Highest Status in ChinaN/A
Originator CompaniesPassage Bio Inc
China Registration ClassN/A

Develop Information

Active CompaniesGemma Biotherapeutics Inc
Inactive CompaniesN/A
Active IndicationsGangliosidosis, GM1Hereditary Central Nervous System Demyelinating Diseases
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A