SRD-001

N/A

Report date: 2026/04/28 18:01:34

Base Information

Drug NameSRD-001
Drug Alias NameSRD-001AAV1/SERCA2aAAV-SERCA2a
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector > AAV1 vector
Mechanisms of ActionSarcoplasmic/endoplasmic reticulum calcium ATPase 2 gene transference
TargetsSarcoplasmic/endoplasmic reticulum calcium ATPase 2
Therapy Area/IndicationsHeart Failure, SystolicHeart Failure, DiastolicHeart Failure +[5
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPhase 2 Clinical
Highest Status in ChinaN/A
Originator CompaniesCelladonTargeted Genetics
China Registration ClassN/A

Develop Information

Active CompaniesSardocor Inc
Inactive CompaniesCelladon Corporation
Active IndicationsHeart Failure, SystolicHeart Failure, DiastolicHeart Failure +[4
Inactive IndicationsCardiomyopathies

Other Information

ATC CodeN/A
Related LinksN/A