AAV-RDH12

N/A

Report date: 2025/03/25 14:45:50

Base Information

Drug NameAAV-RDH12
Drug Alias NameAAV-RDH12AAV5-RDH12
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionGene transferenceRetinol dehydrogenase 12 gene transference
TargetsRetinol dehydrogenase 12
Therapy Area/IndicationsRetinal Dystrophies
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesMeiragtx Ltd
China Registration ClassN/A

Develop Information

Active CompaniesMeiragtx Ltd
Inactive CompaniesN/A
Active IndicationsRetinal Dystrophies
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A