PBKR-03

N/A

Report date: 2024/09/10 15:41:16

Base Information

Drug NamePBKR-03
Drug Alias NamePBKR-03
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector > AAVhu68 vector
Mechanisms of ActionGene transferenceGalactocerebrosidase replacements
TargetsGalactocerebrosidase
Therapy Area/IndicationsLeukodystrophy, Globoid Cell
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryCanadaUnited StatesNetherlands +[6] 
CombinationsNo
Global Highest StatusPending (Phase 2 Clinical)
Highest Status in ChinaN/A
Originator CompaniesUniversity Of Pennsylvania
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesGemma Biotherapeutics Inc
Active IndicationsN/A
Inactive IndicationsLeukodystrophy, Globoid Cell

Other Information

ATC CodeN/A
Related LinksN/A