PRX-ASL

N/A

Report date: 2024/10/21 15:47:29

Base Information

Drug NamePRX-ASL

Drug Alias NameModified messenger ribonucleic acid encoding human argininosuccinate lyase enzyme encapsulated into lipid nanoparticlesASL enzyme replacement therapy (nanoparticle vehicle, ASL deficiency)ASL gene therapy (nanoparticle vehicle, ASL deficiency)mRNA encoding human argininosuccinate lyasePRX-ASL +[6]

ClassificationCell and gene therapy > Gene therapy > mRNA

Mechanisms of ActionArgininosuccinate lyase gene transference

TargetsArgininosuccinate lyase

Therapy Area/IndicationsHyperammonemia

Global Approved IndicationsN/A

Approved Indications in ChinaN/A

Original Approved Country/TerritoryN/A

Original Approved DateN/A

Country/TerritoryN/A

CombinationsNo

Global Highest StatusPreclinical

Highest Status in ChinaN/A

Originator CompaniesN/A

China Registration ClassN/A

Develop Information

Active CompaniesN/A

Inactive CompaniesN/A

Active IndicationsHyperammonemia

Inactive IndicationsN/A

Other Information

ATC CodeN/A