Sonpiretigene isteparvovec

N/A

Report date: 2023/10/26 17:03:04

Base Information

Drug NameSonpiretigene isteparvovec
Drug Alias NameMCO-010vMCO-1vMCO-010
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector > AAV2 vector
Mechanisms of ActionEye protein replacements
TargetsEye proteins
Therapy Area/IndicationsRetinitisRetinal DystrophiesRetinal Diseases +[8
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited StatesPuerto Rico
CombinationsNo
Global Highest StatusPhase 2 Clinical
Highest Status in ChinaN/A
Originator CompaniesNanoscope Therapeutics Inc
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsRetinitisRetinal DystrophiesRetinal Diseases +[7
Inactive IndicationsEye Diseases

Other Information

ATC CodeN/A
Related LinksN/A