CAM-GM201

N/A

Report date: 2023/10/26 17:03:01

Base Information

Drug NameCAM-GM201

Drug Alias NameRecombinant adeno-associated viral vector serotype 2/1 encoding human beta-hexosaminidase alpha and beta subunitsRecombinant adeno-associated virus serotype 2/1 vector encoding human beta-hexosaminidase alpha & beta subunits (rAAV2/1 Hex alpha & beta)CAM-GM201

ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector

Mechanisms of ActionProtein O-GlcNAcase gene transference

TargetsProtein O-GlcNAcase

Therapy Area/IndicationsGangliosidoses, GM2

Global Approved IndicationsN/A

Approved Indications in ChinaN/A

Original Approved Country/TerritoryN/A

Original Approved DateN/A

Country/TerritoryN/A

CombinationsNo

Global Highest StatusClinical

Highest Status in ChinaN/A

Originator CompaniesUniversity Of Cambridge

China Registration ClassN/A

Develop Information

Active CompaniesN/A

Inactive CompaniesN/A

Active IndicationsGangliosidoses, GM2

Inactive IndicationsN/A

Other Information

ATC CodeN/A