Lentiviral vector encoding human coagulation factor IX (Fondazione Telethon)

编码人凝血因子IX的慢病毒载体

Report date: 2023/10/26 17:02:26

Base Information

Drug NameLentiviral vector encoding human coagulation factor IX (Fondazione Telethon)
Drug Alias NameN/A
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Lentiviral vector
Mechanisms of ActionFactor IX gene transference
TargetsCoagulation factor IX
Therapy Area/IndicationsHemophilia B
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryN/A
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesFondazione Telethon
China Registration ClassN/A

Develop Information

Active CompaniesFondazione Telethon
Inactive CompaniesN/A
Active IndicationsHemophilia B
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A