ION-260

N/A

Report date: 2022/10/21 11:39:33
NME

Base Information

Drug NameION-260
Drug Alias NameBIIB-132ION-260
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionRNA interferenceAtaxin-3 inhibitors
TargetsAtaxin-3
Therapy Area/IndicationsMachado-Joseph Disease
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited StatesPortugalNetherlands +[6
CombinationsNo
Global Highest StatusPhase 1 Clinical
Highest Status in ChinaN/A
Originator CompaniesIonis Pharmaceuticals Inc
China Registration ClassN/A

Develop Information

Inactive CompaniesBiogen Inc
Active IndicationsMachado-Joseph Disease
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A