mini-CEP290

N/A

Report date: 2023/12/07 15:06:46

Base Information

Drug Namemini-CEP290
Drug Alias NameLeber congenital amaurosis- gene therapy (IVERIC bio)mini-CEP290 Ivericmini-CEP290mini-CEP-290LCA10 +[6] 
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionCentrosomal protein of 290 kDa modulatorsGene transference
TargetsCentrosomal protein of 290 kDa
Therapy Area/IndicationsLeber Congenital Amaurosis
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesUniversity Of Massachusetts Medical School
China Registration ClassN/A

Develop Information

Active CompaniesIveric Bio Inc
Inactive CompaniesN/A
Active IndicationsLeber Congenital Amaurosis
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A