Nizubaglustat

N/A

Report date: 2026/03/04 20:01:44
NME

Base Information

Drug NameNizubaglustat
Drug Alias NameAZ-3102
ClassificationSmall molecules > Heterocyclic drugs
Mechanisms of Actionβ-glucosidase inhibitorsCeramide glucosyltransferase inhibitors
Targetsβ-glucosidaseCeramide glucosyltransferase
Therapy Area/IndicationsLysosomal Storage DiseasesNiemann-Pick Disease, Type CNiemann-Pick Diseases +[5] 
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryCanadaUnited StatesSweden +[15] 
CombinationsNo
Global Highest StatusPhase 3 Clinical
Highest Status in ChinaN/A
Originator CompaniesAmsterdam Umc, Location AmcLeiden University
China Registration ClassN/A

Develop Information

Active CompaniesAzafaros AGAzafaros BV
Inactive CompaniesN/A
Active IndicationsLysosomal Storage DiseasesNiemann-Pick Disease, Type CNiemann-Pick Diseases +[5] 
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A