GB-501

N/A

Report date: 2024/09/06 15:40:47

Base Information

Drug NameGB-501
Drug Alias NameGB-501
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionAlpha-L-iduronidase replacementsGene transference
TargetsAlpha-L-iduronidase
Therapy Area/IndicationsMucopolysaccharidosis I
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryN/A
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesGraybug Vision Inc
China Registration ClassN/A

Develop Information

Active CompaniesGraybug Vision Inc
Inactive CompaniesN/A
Active IndicationsMucopolysaccharidosis I
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A