ATA-100

N/A

Report date: 2024/09/06 10:13:04

Base Information

Drug NameATA-100
Drug Alias NameLGMD2I/R9 gene therapyrAAV9-hFKRPco_miR-208aATA-100GNT0006GNT-0006
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector > AAV9 vector
Mechanisms of ActionRibitol 5-phosphate transferase FKRP gene transferenceGlycosyltransferases replacements
TargetsRibitol 5-phosphate transferase FKRPGlycosyltransferases
Therapy Area/IndicationsLimb girdle muscular dystrophy 2EMuscular Dystrophies, Limb-Girdle
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited StatesDenmarkUnited Kingdom +[4] 
CombinationsNo
Global Highest StatusPhase 2 Clinical
Highest Status in ChinaN/A
Originator CompaniesAtamyo Therapeutics SAS
China Registration ClassN/A

Develop Information

Active CompaniesAtamyo Therapeutics SAS
Inactive CompaniesN/A
Active IndicationsLimb girdle muscular dystrophy 2EMuscular Dystrophies, Limb-Girdle
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A