NGN-103

N/A

Report date: 2023/10/26 16:58:59

Base Information

Drug NameNGN-103
Drug Alias NameNGN-103
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionMajor facilitator superfamily domain-containing protein 8 gene transference
TargetsMajor facilitator superfamily domain-containing protein 8
Therapy Area/IndicationsNeuronal Ceroid-Lipofuscinoses
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryN/A
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesNeurogene Inc
China Registration ClassN/A

Develop Information

Active CompaniesNeurogene Inc
Inactive CompaniesN/A
Active IndicationsNeuronal Ceroid-Lipofuscinoses
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A