VX-522

N/A

Report date: 2026/05/23 20:00:57
NME

Base Information

Drug NameVX-522
Drug Alias NameCFTR mRNA encapsulated by a lipid nanoparticleVX-522
ClassificationSmall molecules > Nucleosides and nucleotide derivtives
Mechanisms of ActionCFTR gene transference
TargetsCystic fibrosis transmembrane conductance regulator
Therapy Area/IndicationsCystic Fibrosis
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryBelgiumCanadaUnited States +[7
CombinationsNo
Global Highest StatusPhase 2 Clinical
Highest Status in ChinaN/A
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsCystic Fibrosis
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A