ADX-038

N/A

Report date: 2026/04/23 20:00:25
NME

Base Information

Drug NameADX-038
Drug Alias NamesiRNA duplex oligonucleotideADX-038
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Small Interfering RNA
Mechanisms of ActionComplement factor B inhibitors
TargetsComplement factor B
Therapy Area/IndicationsC3 glomerulopathyComplement-Mediated DiseasesHemoglobinuria, Paroxysmal +[6
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryCanadaUnited StatesAustralia +[8
CombinationsNo
Global Highest StatusPhase 2 Clinical
Highest Status in ChinaPhase 2 Clinical
Originator CompaniesADARx Pharmaceuticals Inc
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsC3 glomerulopathyComplement-Mediated DiseasesHemoglobinuria, Paroxysmal +[6
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A