ABO-504

N/A

Report date: 2024/09/06 16:56:32

Base Information

Drug NameABO-504
Drug Alias NameABO-504
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionGene transferenceRetinal-specific phospholipid-transporting ATPase ABCA4 replacements
TargetsRetinal-specific phospholipid-transporting ATPase ABCA4
Therapy Area/IndicationsStargardt Disease
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesAbeona Therapeutics Inc
China Registration ClassN/A

Develop Information

Active CompaniesAbeona Therapeutics Inc
Inactive CompaniesN/A
Active IndicationsStargardt Disease
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A