NHR-01

N/A

Report date: 2023/09/22 17:48:43

Base Information

Drug NameNHR-01
Drug Alias NameNHR01NHR-01
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionUpdating
TargetsUpdating
Therapy Area/IndicationsTay-Sachs DiseaseSandhoff DiseaseGangliosidoses, GM2
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryN/A
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsTay-Sachs DiseaseSandhoff DiseaseGangliosidoses, GM2
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A