ION-440

N/A

Report date: 2026/03/26 20:00:17
NME

Base Information

Drug NameION-440
Drug Alias NameION-440
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionGene silencingMethyl-CpG-binding protein 2 inhibitors
TargetsMethyl-CpG-binding protein 2
Therapy Area/IndicationsLubs X-linked mental retardation syndromeGenetic Diseases, X-Linked
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited StatesAustriaFrance +[4] 
CombinationsNo
Global Highest StatusPhase 2 Clinical
Highest Status in ChinaN/A
Originator CompaniesIonis Pharmaceuticals Inc
China Registration ClassN/A

Develop Information

Active CompaniesIonis Pharmaceuticals Inc
Inactive CompaniesN/A
Active IndicationsLubs X-linked mental retardation syndromeGenetic Diseases, X-Linked
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A