MB-217

N/A

Report date: 2023/12/20 18:00:43

Base Information

Drug NameMB-217
Drug Alias NameCL20-4i-EF1alpha- HgammaC-OPTCL20-i4-EF1α-hγc-OPTEx vivo gene therapy(Mustang Bio)Gene-modified CD34+ hematopoietic stem cells therapy(Mustang Bio)Lentiviral genetherapy(Mustang Bio) +[9
ClassificationCell and gene therapy > Gene therapy
Mechanisms of ActionIL-2RG gene transference
TargetsInterleukin-2 receptor subunit gamma
Therapy Area/IndicationsSevere Combined Immunodeficiency
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesMustang Bio Inc
China Registration ClassN/A

Develop Information

Active CompaniesMustang Bio Inc
Inactive CompaniesN/A
Active IndicationsSevere Combined Immunodeficiency
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A