ATP7A gene therapy (Cyprium Therapeutics)

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Report date: 2026/05/22 20:01:29

Base Information

Drug NameATP7A gene therapy (Cyprium Therapeutics)
Drug Alias NameAAV-ATP7A Gene Therapy for Menkes Disease (Cyprium Therapeutics)AAV-ATP7A gene therapy (Cyprium Therapeutics)
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionCopper-transporting ATPase 1 modulatorsGene transference
TargetsCopper-transporting ATPase 1
Therapy Area/IndicationsMenkes Kinky Hair Syndrome
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesEunice Kennedy Shriver National Institute Of Child Health And Human Development
China Registration ClassN/A

Develop Information

Active CompaniesCyprium Therapeutics Inc +[2] 
Inactive CompaniesN/A
Active IndicationsMenkes Kinky Hair Syndrome
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A