Personalized Antisense Oligonucleotide Therapy(University of California)

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Report date: 2024/03/19 20:00:40

Base Information

Drug NamePersonalized Antisense Oligonucleotide Therapy(University of California)
Drug Alias NamePersonalized antisense oligonucleotide(University of California)nL-SCN2A-002
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionUpdating
TargetsUpdating
Therapy Area/IndicationsGenetic Diseases, Inborn
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPhase 2 Clinical
Highest Status in ChinaN/A
Originator CompaniesUniversity Of California
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsGenetic Diseases, Inborn
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A