Stargardt

N/A

Report date: 2024/05/13 16:58:24

Base Information

Drug NameStargardt
Drug Alias NameSGT-1001
ClassificationCell and gene therapy > Gene therapy
Mechanisms of ActionRetinal-specific phospholipid-transporting ATPase ABCA4 gene transference
TargetsRetinal-specific phospholipid-transporting ATPase ABCA4
Therapy Area/IndicationsRetinal Diseases
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesSaliogen Therapeutics Inc
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsRetinal Diseases
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A