ED-001

N/A

Report date: 2024/09/19 13:54:06

Base Information

Drug NameED-001
Drug Alias NameED-001
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Herpes simplex virus vector
Mechanisms of ActionRetinal-specific phospholipid-transporting ATPase ABCA4 gene transference
TargetsRetinal-specific phospholipid-transporting ATPase ABCA4
Therapy Area/IndicationsStargardt Disease
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesReplay Holdings LLC
China Registration ClassN/A

Develop Information

Active CompaniesReplay Holdings LLC
Inactive CompaniesN/A
Active IndicationsStargardt Disease
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A