PAH gene modulator LNP based AAV gene therapy (I-PGI)

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Report date: 2024/05/30 17:46:55

Base Information

Drug NamePAH gene modulator LNP based AAV gene therapy (I-PGI)
Drug Alias NameN/A
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionPhenylalanine hydroxylase modulators
TargetsPhenylalanine hydroxylase
Therapy Area/IndicationsPhenylketonuriasHomocystinuria
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesTome Biosciences Inc
China Registration ClassN/A

Develop Information

Active CompaniesTome Biosciences Inc
Inactive CompaniesN/A
Active IndicationsPhenylketonuriasHomocystinuria
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A