Gene-modified CD34+ cells therapy(St. Jude Children'S Research Hospital)

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Report date: 2025/08/14 17:46:55

Base Information

Drug NameGene-modified CD34+ cells therapy(St. Jude Children'S Research Hospital)
Drug Alias NameN/A
ClassificationCell and gene therapy > Gene therapy > Gene editing > CRISPR > CRISPR-Cas9Cell and gene therapy > Cell therapy > Stem cell therapy > Hematopoietic stem cells therapy
Mechanisms of ActionStem cell replacementsFetal hemoglobin modulators
TargetsFetal hemoglobin
Therapy Area/IndicationsAnemia, Sickle Cell
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPhase 1 Clinical
Highest Status in ChinaN/A
Originator CompaniesSt. Jude Children'S Research Hospital
China Registration ClassN/A

Develop Information

Active CompaniesSt. Jude Children'S Research Hospital
Inactive CompaniesN/A
Active IndicationsAnemia, Sickle Cell
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A