GENE-202

N/A

Report date: 2025/05/16 17:55:14

Base Information

Drug NameGENE-202
Drug Alias NameGENE202GENE-202
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Lentiviral vector
Mechanisms of ActionMethylmalonyl-CoA Mutase gene transference
TargetsMethylmalonyl-CoA Mutase
Therapy Area/IndicationsMethylmalonic acidaemiaFibrolamellar hepatocellular carcinoma
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryItaly
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesGenespire SRL
China Registration ClassN/A

Develop Information

Active CompaniesGenespire SRL
Inactive CompaniesN/A
Active IndicationsMethylmalonic acidaemiaFibrolamellar hepatocellular carcinoma
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A