ABO-301

N/A

Report date: 2024/11/20 13:54:53

Base Information

Drug NameABO-301
Drug Alias NameABO-301
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionFanconi anemia group C protein gene transference
TargetsFanconi anemia group C protein
Therapy Area/IndicationsFanconi Anemia
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesAbeona Therapeutics Inc
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesAbeona Therapeutics Inc
Active IndicationsN/A
Inactive IndicationsFanconi Anemia

Other Information

ATC CodeN/A
Related LinksN/A