DT-216

N/A

Report date: 2025/06/13 11:09:49
NME

Base Information

Drug NameDT-216
Drug Alias NameDT-216P2DT-216Syn TEF1
ClassificationSmall molecules > Heterocyclic drugs
Mechanisms of ActionFrataxin Gene transferenceGenetic transcription stimulants
TargetsFrataxin, mitochondrial
Therapy Area/IndicationsFriedreich Ataxia
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited StatesAustralia
CombinationsNo
Global Highest StatusPhase 2 Clinical
Highest Status in ChinaN/A
Originator CompaniesDesign Therapeutics Inc
China Registration ClassN/A

Develop Information

Active CompaniesDesign Therapeutics Inc
Inactive CompaniesN/A
Active IndicationsFriedreich Ataxia
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A