ARO-ATXN1

N/A

Report date: 2025/01/22 16:58:38
NME

Base Information

Drug NameARO-ATXN1
Drug Alias NameARO-ATXN1
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Small Interfering RNA
Mechanisms of ActionRNA interferenceAtaxin 1 modulators
TargetsAtaxin 1
Therapy Area/IndicationsSpinocerebellar Ataxias
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesArrowhead Pharmaceuticals Inc
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsSpinocerebellar Ataxias
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A