AAVrh.10-mNpc2-HA

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Report date: 2024/12/19 13:28:42

Base Information

Drug NameAAVrh.10-mNpc2-HA
Drug Alias NameAAVrh.10-mNpc2-HA
ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionNPC intracellular cholesterol transporter 2 gene transference
TargetsNPC intracellular cholesterol transporter 2
Therapy Area/IndicationsNiemann-Pick Disease, Type C2
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPending (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesWeill Cornell Medical College
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesWeill Cornell Medical College
Active IndicationsN/A
Inactive IndicationsNiemann-Pick Disease, Type C2

Other Information

ATC CodeN/A
Related LinksN/A