AX-4070

N/A

Report date: 2025/01/07 15:03:07
NME

Base Information

Drug NameAX-4070
Drug Alias NameAX-4070
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide
Mechanisms of ActionMethyl-CpG-binding protein 2 modulators
TargetsMethyl-CpG-binding protein 2
Therapy Area/IndicationsCentral Nervous System Diseases
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryN/A
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesProqr Therapeutics Nv
China Registration ClassN/A

Develop Information

Active CompaniesProqr Therapeutics Nv
Inactive CompaniesN/A
Active IndicationsCentral Nervous System Diseases
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A