ASAH1 gene therapy (Genethon)

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Report date: 2025/01/22 10:49:13

Base Information

Drug NameASAH1 gene therapy (Genethon)
Drug Alias NameN/A
ClassificationCell and gene therapy > Gene therapy
Mechanisms of ActionAcid ceramidase gene transference
TargetsAcid ceramidase
Therapy Area/IndicationsMuscular Atrophy, SpinalFarber Lipogranulomatosis
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryFrance
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesGenethon
China Registration ClassN/A

Develop Information

Active CompaniesGenethon
Inactive CompaniesN/A
Active IndicationsMuscular Atrophy, SpinalFarber Lipogranulomatosis
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A