Antisense oligonucleotide therapy ( Cure Rare Disease)

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Report date: 2025/02/11 11:51:28
NME

Base Information

Drug NameAntisense oligonucleotide therapy ( Cure Rare Disease)
Drug Alias NameN/A
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionAntisense oligonucleotide inhibitors
TargetsUpdating
Therapy Area/IndicationsMachado-Joseph Disease
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesCure Rare Disease
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsMachado-Joseph Disease
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A