TX-01(Theranexus)

N/A

Report date: 2026/02/12 20:00:14
NME

Base Information

Drug NameTX-01(Theranexus)
Drug Alias NameTX-01TX-01(Theranexus)
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionUpdating
TargetsUpdating
Therapy Area/IndicationsNiemann-Pick Disease, Type CGaucher Disease
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryFrance
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesTheranexus
China Registration ClassN/A

Develop Information

Active CompaniesTheranexusBiocodex Sa
Inactive CompaniesN/A
Active IndicationsNiemann-Pick Disease, Type CGaucher Disease
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A