GENV-002

N/A

Report date: 2025/08/21 17:31:02

First In Class

Base Information

Drug NameGENV-002

Drug Alias NameGENV-002 (AAV.GAA and AAV.Cas9)GENV-002

ClassificationCell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adenoviral vectorCell and gene therapy > Gene therapy > Gene editing > CRISPR > CRISPR-Cas9

Mechanisms of ActionAlpha-glucosidases modulators

TargetsAlpha-glucosidases

Therapy Area/IndicationsGlycogen Storage Disease Type II

Global Approved IndicationsN/A

Approved Indications in ChinaN/A

Original Approved Country/TerritoryN/A

Original Approved DateN/A

Country/TerritoryUnited States

CombinationsNo

Global Highest StatusPreclinical

Highest Status in ChinaN/A

Originator CompaniesGeneVentiv Therapeutics Inc

China Registration ClassN/A

Develop Information

Active CompaniesGeneVentiv Therapeutics Inc

Inactive CompaniesN/A

Active IndicationsGlycogen Storage Disease Type II

Inactive IndicationsN/A

Other Information

ATC CodeN/A