UBE3A antisense oligonucleotide (Quiver Bioscience)

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Report date: 2025/06/27 16:57:40
NME

Base Information

Drug NameUBE3A antisense oligonucleotide (Quiver Bioscience)
Drug Alias NameDup15q Syndrome-UBE3A (ASO)
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionUbiquitin-like modifier-activating enzyme 3A modulators
TargetsUbiquitin-like modifier-activating enzyme 3A
Therapy Area/IndicationsDup15q syndrome
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesQuiver Bioscience Inc
China Registration ClassN/A

Develop Information

Active CompaniesQuiver Bioscience Inc
Inactive CompaniesN/A
Active IndicationsDup15q syndrome
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A