GB-221 (GEMMA Biotherapeutics)

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Report date: 2026/03/04 20:01:44

Base Information

Drug NameGB-221 (GEMMA Biotherapeutics)
Drug Alias NameGB-221
ClassificationCell and gene therapy > Gene therapy
Mechanisms of ActionSMN gene transference
TargetsSurvival motor neuron protein
Therapy Area/IndicationsSpinal Muscular Atrophies of Childhood
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited StatesBrazil
CombinationsNo
Global Highest StatusPhase 2 Clinical
Highest Status in ChinaN/A
Originator CompaniesGemma Biotherapeutics Inc
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsSpinal Muscular Atrophies of Childhood
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A