Gene editing therapy for primary hyperoxaluria tipe I (University of Navarra)

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Report date: 2025/09/05 14:00:01

Base Information

Drug NameGene editing therapy for primary hyperoxaluria tipe I (University of Navarra)
Drug Alias NameN/A
ClassificationCell and gene therapy > Gene therapy > Gene editing > CRISPR > CRISPR-Cas9Cell and gene therapy > Gene therapy > Viral vector-based gene therapy > Adeno-associated virus vector
Mechanisms of ActionUpdating
TargetsUpdating
Therapy Area/IndicationsHyperoxaluria
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritorySpain
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesUniversity Of Navarra
China Registration ClassN/A

Develop Information

Active CompaniesUniversity Of Navarra
Inactive CompaniesN/A
Active IndicationsHyperoxaluria
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A