PRO-135

N/A

Report date: 2022/01/22 15:45:59
NME

Base Information

Drug NamePRO-135
Drug Alias NamePRO-135
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionDystrophin pre-mRNA modulators
TargetsDystrophin pre-mRNA
Therapy Area/IndicationsMyotonic Dystrophy
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryN/A
CombinationsNo
Global Highest StatusDiscontinued (Preclinical)
Highest Status in ChinaN/A
Originator CompaniesBiomarin Pharmaceutical Inc
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Inactive CompaniesBiomarin Pharmaceutical Inc
Active IndicationsN/A
Inactive IndicationsMyotonic Dystrophy

Other Information

ATC CodeN/A
Related LinksN/A