Glygogen Storage Disease Type 1a therapy(Genethon)

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Report date: 2025/10/31 09:42:07

Base Information

Drug NameGlygogen Storage Disease Type 1a therapy(Genethon)
Drug Alias NameGSD1a therapy(Genethon)
ClassificationCell and gene therapy > Gene therapy
Mechanisms of ActionGlucose-6-phosphatase modulators
TargetsGlucose-6-phosphatase
Therapy Area/IndicationsGlycogen Storage Disease Type I
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryFrance
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesGenethon
China Registration ClassN/A

Develop Information

Active CompaniesInstitut National De La Sante Et De La Recherche MedicaleGenethon
Inactive CompaniesN/A
Active IndicationsGlycogen Storage Disease Type I
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A