nL-GARS1-001

N/A

Report date: 2025/11/12 20:00:48
NME

Base Information

Drug NamenL-GARS1-001
Drug Alias NamenL-GARS1-001
ClassificationSmall molecules > Nucleosides and nucleotide derivtives > Oligonucleotide > Oligonucleotide antisense
Mechanisms of ActionUpdating
TargetsUpdating
Therapy Area/IndicationsCharcot-Marie-Tooth Disease
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPhase 2 Clinical
Highest Status in ChinaN/A
Originator CompaniesN-Lorem Foundation
China Registration ClassN/A

Develop Information

Active CompaniesN-Lorem Foundation
Inactive CompaniesN/A
Active IndicationsCharcot-Marie-Tooth Disease
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A