PM647

N/A

Report date: 2025/12/17 17:47:42

Base Information

Drug NamePM647
Drug Alias NamePM-647
ClassificationCell and gene therapy > Gene therapy > LNP
Mechanisms of ActionUpdating
TargetsUpdating
Therapy Area/Indicationsalpha 1-Antitrypsin Deficiency
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesPrime Medicine Inc
China Registration ClassN/A

Develop Information

Active CompaniesPrime Medicine Inc
Inactive CompaniesN/A
Active Indicationsalpha 1-Antitrypsin Deficiency
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A