Small molecule for myotonic dystrophy type 1 (Vertex Pharmaceuticals)

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Report date: 2025/12/25 11:27:31
NME

Base Information

Drug NameSmall molecule for myotonic dystrophy type 1 (Vertex Pharmaceuticals)
Drug Alias NameSmall molecule for DM1 (Vertex Pharmaceuticals)
ClassificationSmall molecules > Heterocyclic drugs
Mechanisms of ActionUpdating
TargetsUpdating
Therapy Area/IndicationsMyotonic Dystrophy
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryUnited States
CombinationsNo
Global Highest StatusPreclinical
Highest Status in ChinaN/A
Originator CompaniesVertex Pharmaceuticals Gmbh
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsMyotonic Dystrophy
Inactive IndicationsN/A

Other Information

ATC CodeN/A
Related LinksN/A